Topic: Rare diseases

Seminar
9 seminars
Conference
1 conference
Job
1 job
Conference

European Human Genetics Conference 2027

Rotterdam, The Netherlands
Jun 12, 2027

The 60th European Human Genetics Conference of the European Society of Human Genetics, held June 12-15, 2027 in Rotterdam, The Netherlands as a hybrid conference with in-person and virtual participation.

JobComputational Biology

Bioinformatics Developer

Hinxton, Cambridgeshire, United Kingdom
Sep 22, 2026

EMBL-EBI seeks a Bioinformatics Developer for DECIPHER, a platform supporting rare-disease research and clinical interpretation of genetic variation. The developer will evaluate and integrate genomic and phenotype resources, deploy analysis tools, design database structures and interfaces, investigate data problems and work with clinical and research collaborators. The role is based in Hinxton with hybrid working and may be full time or 80% time. The advert gives a closing date of 8 October 2026 at 23:59 CET.

SeminarDevelopmental Neuroscience

Expanding the role of MAST kinases in brain development and epilepsy: identification of de novo pathogenic variants in MAST4

Kimberly Aldinger
University of Washington; Seattle Children's Research Institute
Apr 19, 2023
SeminarMedicineRecording

Improving care for rare disease patients in Europe - Rare Disease Day 2021

Holm Graessner Donna Walsh Sophie Bernichtein Tobias Mentzel Maria Judit Molnar
ERN-RND EFNA BRAIN-TEAM ELA Germany Semmelweis University
Feb 23, 2021
SeminarMedicine

Lysosomal storage disorders and their unanticipated links to rare and common diseases

Frances Platt
University of Oxford
Feb 8, 2021

Lysosomal storage diseases are a group of over 70 inherited metabolic disorders, many of which have a neurodegenerative clinical course. Treatments have been developed for a subset of these disorders and are now in routine clinical use. We have found that some neurological and neurodegenerative diseases share unanticipated links to lysosomal storage diseases providing insights into disease pathogenesis. These links also suggest treatments developed for lysosomal disorders may have unanticipated utility in other rare and common diseases.

SeminarMedicineRecording

Treatment of spasticity in HSP and leukodystrophies

Annemieke Buizer
Amsterdam Research Institute for Movement Sciences & Amsterdam University Medical Center, Netherlands
Oct 6, 2020
SeminarMedicineRecording

Hereditary Spastic Paraplegia (HSP): clinical disease course

Rebecca Schüle
University of Tübingen, Germany
Oct 1, 2020
SeminarMedicineRecording

How can we develop and implement evidence based rehabilitation in rare disorders?

Hortensia Gimeno
NIHR & Guy's and St Thomas' NHS Foundation Trust, UK
Sep 29, 2020
SeminarGeneticsRecording

A challenge in neurogenetics: Huntington disease in kids

Ferdinando Squitieri
Fondazione IRCCS Casa Sollievo Sofferenza & CSS-Mendel Institute, Italy
Sep 15, 2020
SeminarMedicineRecording

How to assess and manage spastic gait in rare diseases?

Gál Ota
General University Hospital in Prague, Czech Republic
Sep 10, 2020
SeminarNeuroscienceRecording

Semantic variant of primary progressive aphasia, clinical manifestation and underlying neuropathology

Robert Rusina & Zsolt Cséfalvay
Charles University Thomayer Hospital & Comenius University, Czech Republic
Sep 8, 2020

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