Targeting alternative splicing of SYNGAP1 using antisense oligonucleotides
Video · 25 min · Captions · Sep 29, 2022
Benjamin Prosser, University of Pennsylvania Perelman School of Medicine, PhD
Antisense oligonucleotide mediated exon skipping therapy development for Duchenne muscular dystrophy takes more than an oligonucleotide
Pharmacology, Biotechnology, Clinical Neurology and seminar by Annemieke Aartsma-Rus, Leiden University Medical Center, the Netherlands
Hosted by ERN-RND
Tuesday 15:00–16:10 London (GMT+1)
Recording available
Online
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