Targeting alternative splicing of SYNGAP1 using antisense oligonucleotides
Video · 25 min · Captions · Sep 29, 2022
Benjamin Prosser, University of Pennsylvania Perelman School of Medicine, PhD
ASO RNA splice modulating therapies for genetic brain disorders
Medical Genetics, Clinical Neurology, Neuropharmacology and seminar by Willeke van Roon-Mom, University of Leiden, the Netherlands
Hosted by ERN-RND
Tuesday 14:00–15:10 London (GMT+0)
Recording available
Online
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